Treatment Gene Therapy Gene therapy is a technique used in an effort to treat or prevent disease. Find a Doctor See Related Programs
Condition Spinal Muscular Atrophy (SMA) Spinal muscular atrophy is when muscles throughout the body are weakened because nerve cells in the spinal cord and brainstem do not work properly. Find a Doctor See Related Programs
Treatment Zolgensma Zolgensma® (onasemnogene abeparvovec-xioi) is a gene therapy for spinal muscular atrophy (SMA) in children under 2. Find a Doctor See Related Programs
